Latest Alagille syndrome Stories

2014-05-09 08:26:09

CAMEO Phase 2 Clinical Trial of LUM001 Now Enrolling Adults with Primary Sclerosing Cholangitis SAN DIEGO, May 9, 2014 /PRNewswire/ -- Lumena Pharmaceuticals (Lumena), a biopharmaceutical company focused on the development and commercialization of novel products for rare cholestatic liver diseases and serious metabolic disorders, today announced the dosing of the first patient in the INDIGO Phase 2 clinical trial of its lead drug candidate, LUM001, in children with progressive...

2013-06-06 23:01:33

Stories of Hope, Success and Progress Illustrate Need for Collaboration With Patients Horsham, Pa. (PRWEB) June 06, 2013 Utah Assistant Attorney General and spinal muscular atrophy survivor Steve Mikita and five other inspiring patient advocates will share stories of their tireless efforts to insert the patient voice at each step of the drug development process at the DIA 2013 49th Annual Meeting in Boston this month. The news media are invited to listen to the compelling stories of these...

Same Musicians Play Brand New Tune
2013-05-15 07:54:37

Stowers Institute for Medical Research A small ensemble of musicians can produce an infinite number of melodies, harmonies and rhythms. So too, do a handful of workhorse signaling pathways that interact to construct multiple structures that comprise the vertebrate body. In fact, crosstalk between two of those pathways–those governed by proteins known as Notch and BMP (for Bone Morphogenetic Protein) receptors–occurs over and over in processes as diverse as forming a tooth,...

2013-02-13 17:35:32

Researchers from the University of Pennsylvania School of Veterinary Medicine have discovered that a protein called Jagged-1 stimulates human stem cells to differentiate into bone-producing cells. This protein could help both human and animal patients heal from bone fractures faster and may form the basis of treatments for a rare metabolic condition called Alagille syndrome. The study, published in the journal Stem Cells, was authored by three members of Penn Vet´s departments of...

Word of the Day
  • A fool; a simpleton: a term of abuse common in Ireland and to a less extent in the Gaelic-speaking parts of Scotland.
This word is partly Irish in origin.