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Latest Becker's muscular dystrophy Stories

2009-12-08 07:00:00

SOUTH PLAINFIELD, N.J., Dec. 8 /PRNewswire/ -- Data published online in the medical journal Muscle and Nerve support the use of the six-minute walk test (6MWT) as an outcome measure in PTC Therapeutics, Inc.'s ongoing registration-directed clinical trial of ataluren in patients with nonsense mutation Duchenne/Becker muscular dystrophy (nmDMD/BMD). The study results, which will also be published in an upcoming print issue of the journal, characterize the limitations on walking by patients...

2009-11-11 00:00:00

AMSTERDAM, November 11 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext: AMT), a leader in the field of human gene therapy, announced today that it has successfully treated Duchenne muscular dystrophy (DMD) in an animal model with its proprietary gene therapy. The proof of concept studies were performed in collaboration with the group of Professor Irene Bozzoni (University of Rome, La Sapienza, Italy) and demonstrated effectiveness in the heart as well as in skeletal...

2009-11-06 09:32:00

Dr. Carmen Bertoni to Receive $75,000 For Duchenne Muscular Dystrophy Research MIDDLETOWN, Ohio, Nov. 6 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced today the latest recipient of the End Duchenne Grant Award Program. Carmen Bertoni, Ph.D., Assistant Professor of the Department...

2009-10-26 07:00:00

SOUTH PLAINFIELD, N.J., Oct. 26 /PRNewswire/ -- PTC Therapeutics, Inc. (PTC) today announced it is expanding the development of ataluren, an investigational new drug, to a third indication with the initiation of a Phase 2a clinical trial in nonsense mutation hemophilia A (nmHA) and hemophilia B (nmHB). Hemophilia is a rare and debilitating genetic disorder that causes loss of blot clotting proteins and can lead to serious, recurrent bleeding episodes. It is estimated that nonsense...

2009-10-16 10:26:00

DALLAS, Oct. 16 /PRNewswire-USNewswire/ -- John Killian, Chairman of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), and his wife Stefanie Killian, announced today that the 5th Annual Sam's Family Fun Day (Sam's Day) will take place on October 24, 2009 from 10am to 2pm on Flagpole Hill at White Rock Lake. (Photo: http://www.newscom.com/cgi-bin/prnh/20091016/DC93763)...

2009-10-13 00:00:00

AMSTERDAM, October 13 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext: AMT), a leader in the field of human gene therapy, announced today that the European Medicines Agency has granted Orphan Drug Designation to AMT's gene therapy product AMT-080 for the treatment of Duchenne muscular dystrophy. Orphan Drug Designation for Duchenne muscular dystrophy (DMD) entitles AMT to ten year market exclusivity in Europe following marketing approval for AMT-080 if this...

2009-09-29 06:00:00

Duchenne Organization Competes With Over 500 Nonprofits To Win Grand Prize MIDDLETOWN, Ohio, Sept. 29 /PRNewswire-USNewswire/ -- Intel, as Sponsors of Tomorrow(TM), announced Parent Project Muscular Dystrophy (PPMD) as the winner of its Vote For A Cause contest on its Facebook Page. Over 600 nonprofit organizations were nominated and based upon online voting by Facebook members, organizations were eliminated through five rounds of competition. PPMD is the recipient of $50,000 in...

2009-06-24 08:04:41

A group led by Dr. Paul T. Martin of The Ohio State University College of Medicine has demonstrated that the glycosyltransferase Galgt2 can lessen symptoms in multiple models of muscular dystrophy. Their report can be found in the July 2009 issue of the American Journal of Pathology.Muscular dystrophy is a group of inherited muscular disorders that are characterized by progressive skeletal muscle weakness, defects in muscle proteins, and the death of muscle cells and tissue. Recent studies...

2009-06-22 13:51:00

Senator Johnny Isakson, American Football Coaches Association to Receive Awards MIDDLETOWN, Ohio, June 22 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that PPMD will be honoring United States Senator Johnny Isakson and the American Football Coaches Association (AFCA) with...

2009-06-18 12:36:10

British medical scientists say they used an animal study to demonstrate a method of making an early diagnosis of muscular dystrophy, before symptoms develop. University of Birmingham researchers said they used mice to study the key proteins involved in two types of muscular dystrophy -- Duchenne muscular dystrophy and a milder form, Limb Girdle MD. The researchers said they identified disrupted stem cell function and delays of skeletal muscle formation in embryos of muscular dystrophy-like...


Word of the Day
vermicular
  • Like a worm in form or movement; vermiform; tortuous or sinuous; also, writhing or wriggling.
  • Like the track or trace of a worm; appearing as if worm-eaten; vermiculate.
  • Marked with fine, close-set, wavy or tortuous lines of color; vermiculated.
  • A form of rusticated masonry which is so wrought as to appear thickly indented with worm-tracks.
This word ultimately comes from the Latin 'vermis,' worm.
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