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Latest Becker's muscular dystrophy Stories

2011-03-06 23:59:00

AMSTERDAM, March 7, 2011 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (AMT) (Euronext: AMT), a leader in the field of human gene therapy, announced today that the Duchenne Parent Project, based in the Netherlands, has awarded AMT a grant of EUR 145,000 to support the development of AMT-080, AMT's gene therapy for Duchenne Muscular Dystrophy (DMD). DMD is a severe, fatal disease affecting young children, almost exclusively boys, characterized by progressive muscle...

2011-02-08 10:14:00

Efforts over decade result in $192 million in Duchenne-specific federal investment HACKENSACK, N.J., Feb. 8, 2011 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne) - will host their annual Advocacy Conference, including the One Voice Advocacy Summit, in Washington, D.C. from February 13 - 15, 2011. (Logo:...

2011-02-04 12:48:21

It's a gene called DOT1L, and if you don't have enough of the DOT1L enzyme, you could be at risk for some types of heart disease. These findings by UNC researchers appear in the Feb. 1, 2011 issue of the journal Genes and Development. Everyone knows chocolate is critical to a happy Valentine's Day. Now scientists are one step closer to knowing what makes a heart happy the rest of the year. It's a gene called DOT1L, and if you don't have enough of the DOT1L enzyme, you could be at risk for...

2011-02-01 12:00:00

SOUTH PLAINFIELD, N.J. and HACKENSACK, N.J., Feb. 1, 2011 /PRNewswire/ -- PTC Therapeutics, Inc. (PTC) and Parent Project Muscular Dystrophy (PPMD) today announced an expansion of their collaboration to discover new treatments for patients with Duchenne/Becker muscular dystrophy (DBMD). PPMD has awarded PTC a $250,000 grant, with the potential of additional funding, to advance drug discovery efforts in identifying a new treatment that improves heart function in patients with DBMD. (Logo:...

2010-12-27 20:41:24

A novel potential therapy based on a natural human protein significantly slows muscle damage and improves function in mice who have the same genetic mutation as boys with the most common form of muscular dystrophy, according to a paper published online Dec. 27 in the Proceedings of the National Academy of Sciences. Duchenne Muscular Dystrophy is a fatal genetic mutation in about one of every 3,500 boys. They are unable to produce a protein called dystrophin that keeps muscles strong. By eight...

2010-12-21 07:00:00

SOUTH PLAINFIELD, N.J., Dec. 21, 2010 /PRNewswire/ -- PTC Therapeutics, Inc. announced today that it has completed enrollment of a Phase 3 clinical trial of ataluren, an investigational new drug, in patients with nonsense mutation cystic fibrosis (nmCF). (Logo: http://photos.prnewswire.com/prnh/20010919/PTCLOGO ) The 48-week study is designed to determine whether ataluren can improve lung function in patients with nmCF. The trial has enrolled 238 patients at 36 sites in North America,...

2010-12-01 07:00:00

SOUTH PLAINFIELD, N.J., Dec. 1, 2010 /PRNewswire/ -- Data published in the December issue of the medical journal Muscle and Nerve confirm the utility of six-minute walk distance (6MWD) as a clinically meaningful endpoint in dystrophinopathy, a disease continuum comprising Duchenne and Becker muscular dystrophy (DBMD). The data showed that boys with DBMD experience a significant decline in walking ability compared to healthy boys over one year, suggesting that slowing the loss of walking...

2010-11-10 11:00:00

HACKENSACK, N.J., Nov. 10, 2010 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that Founding President and CEO Patricia Furlong was named one of WebMD's 2010 Health Heroes. (Logo: http://photos.prnewswire.com/prnh/20100119/DC39975LOGO) (Logo: http://www.newscom.com/cgi-bin/prnh/20100119/DC39975LOGO) Ms. Furlong is one of six...

2010-11-02 08:10:10

(Ivanhoe Newswire) -- Muscular dystrophies or MD are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. New research is now helping establish a new and unifying model for the cause of a common type of MD called facioscapulohumeral dystrophy. Facioscapulohumeral refers to the muscles that move the face, shoulder blade, and upper arm bone. This form of muscular dystrophy appears in the teens to early...

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2010-10-19 09:25:00

Viagra, the famous little blue pill that millions of men use for erectile dysfunction, and originally developed to help ailing hearts, may now also help treat heart symptoms of muscular dystrophy, according to researchers Monday. Mice that were genetically engineered to have a condition similar to Duchenne muscular dystrophy were tested and scientists found the drug could improve how the heart works, according to their research. Joseph Beavoa of the University of Washington and colleagues...


Word of the Day
virgule
  • A punctuation mark (/) used to separate related items of information.
  • A little rod; a twig.
This word comes from the Late Latin 'virgula,' accentual mark, a diminutive of 'virga,' rod.
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