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Latest Becker's muscular dystrophy Stories

2010-12-21 07:00:00

SOUTH PLAINFIELD, N.J., Dec. 21, 2010 /PRNewswire/ -- PTC Therapeutics, Inc. announced today that it has completed enrollment of a Phase 3 clinical trial of ataluren, an investigational new drug, in patients with nonsense mutation cystic fibrosis (nmCF). (Logo: http://photos.prnewswire.com/prnh/20010919/PTCLOGO ) The 48-week study is designed to determine whether ataluren can improve lung function in patients with nmCF. The trial has enrolled 238 patients at 36 sites in North America,...

2010-12-01 07:00:00

SOUTH PLAINFIELD, N.J., Dec. 1, 2010 /PRNewswire/ -- Data published in the December issue of the medical journal Muscle and Nerve confirm the utility of six-minute walk distance (6MWD) as a clinically meaningful endpoint in dystrophinopathy, a disease continuum comprising Duchenne and Becker muscular dystrophy (DBMD). The data showed that boys with DBMD experience a significant decline in walking ability compared to healthy boys over one year, suggesting that slowing the loss of walking...

2010-11-10 11:00:00

HACKENSACK, N.J., Nov. 10, 2010 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that Founding President and CEO Patricia Furlong was named one of WebMD's 2010 Health Heroes. (Logo: http://photos.prnewswire.com/prnh/20100119/DC39975LOGO) (Logo: http://www.newscom.com/cgi-bin/prnh/20100119/DC39975LOGO) Ms. Furlong is one of six...

2010-11-02 08:10:10

(Ivanhoe Newswire) -- Muscular dystrophies or MD are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. New research is now helping establish a new and unifying model for the cause of a common type of MD called facioscapulohumeral dystrophy. Facioscapulohumeral refers to the muscles that move the face, shoulder blade, and upper arm bone. This form of muscular dystrophy appears in the teens to early...

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2010-10-19 09:25:00

Viagra, the famous little blue pill that millions of men use for erectile dysfunction, and originally developed to help ailing hearts, may now also help treat heart symptoms of muscular dystrophy, according to researchers Monday. Mice that were genetically engineered to have a condition similar to Duchenne muscular dystrophy were tested and scientists found the drug could improve how the heart works, according to their research. Joseph Beavoa of the University of Washington and colleagues...

2010-10-15 07:00:00

SOUTH PLAINFIELD, N.J., Oct. 15 /PRNewswire/ -- PTC Therapeutics, Inc. today announced that final analyses of Phase 2b efficacy data suggest the investigational new drug ataluren slowed the loss of walking ability in patients with nonsense mutation dystrophinopathy, a disease continuum comprising Duchenne and Becker muscular dystrophy (nmDBMD). These data were presented at the International Congress of the World Muscle Society in Kumamoto, Japan and will be the basis of interactions...

2010-10-08 01:58:14

Natural immunity to dystrophin may contribute to muscle disease and complicate experimental therapies An immune reaction to dystrophin, the muscle protein that is defective in patients with Duchenne muscular dystrophy, may pose a new challenge to strengthening muscles of patients with this disease, suggests a new study appearing in the October 7, 2010, issue of The New England Journal of Medicine. Duchenne muscular dystrophy (DMD) is a hereditary and lethal neuromuscular disease characterized...

2010-10-05 11:00:00

After 5 Years at White Rock Lake, Local Outreach Effort and Fundraiser Moves to a Larger Stage DALLAS, Oct. 5 /PRNewswire-USNewswire/ -- John Killian, Chairman of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), and his wife Stefanie Killian, announced today that the 6th Annual Sam's Day will take place on October 30, 2010 from 11am to 5pm at NorthPark Center in Dallas....

2010-09-24 01:00:00

AMSTERDAM, September 24, 2010 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (AMT) Holding N.V. (Euronext: AMT), a leader in the field of human gene therapy, announced today that the U.S. Food and Drug Administration (FDA) has designated AMT-080, a gene therapy for Duchenne muscular dystrophy (DMD) as an orphan drug. In October 2009, the Committee for Orphan Medical Products of the European Medicines Agency granted AMT-080 orphan designation for the same indication in the...

2010-09-03 07:47:00

$11 Million Supports Five-Year Study to Compare Treatments ROCHESTER, N.Y., Sept. 3 /PRNewswire-USNewswire/ -- A large international study aimed at improving the care of muscular dystrophy patients worldwide is being launched by physicians, physical therapists, and researchers at the University of Rochester Medical Center. Neurologist Robert "Berch" Griggs, M.D., is heading the study of treatments for Duchenne muscular dystrophy, the most common form of the disease that affects children....