Latest Duchenne muscular dystrophy Stories
Duchenne muscular dystrophy affects 1 in every 3,600 male infants each year. Due to the way the disease is inherited, girls are not affected. Muscular dystrophy consists of a group of inherited disorders causing muscle weakness and loss of muscle tissue, which progressively becomes worse.
The challenge of treating patients with genetic disorders in which a single mutated gene is simply too large to be replaced using traditional gene therapy techniques may soon be a thing of the past.
- Growing in low tufty patches.