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Last updated on April 24, 2014 at 1:21 EDT

Latest Duchenne muscular dystrophy Stories

2010-09-28 11:51:00

SCOTTSDALE, Ariz., Sept. 28 /PRNewswire/ -- Scottsdale-based software and interactive media firm, Jawa, is pleased to announce its participation in the Muscular Dystrophy Association Lock Up, a unique fundraising event in which local community leaders are 'arrested' and put in MDA jail for having a big heart. Two Jawa staff members were nominated to go behind bars for the September 22 Lock Up event and posted maximum bail, courtesy of Jawa. The bail money will help send Phoenix-area...

2010-09-24 01:00:00

AMSTERDAM, September 24, 2010 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (AMT) Holding N.V. (Euronext: AMT), a leader in the field of human gene therapy, announced today that the U.S. Food and Drug Administration (FDA) has designated AMT-080, a gene therapy for Duchenne muscular dystrophy (DMD) as an orphan drug. In October 2009, the Committee for Orphan Medical Products of the European Medicines Agency granted AMT-080 orphan designation for the same indication in the...

2010-09-09 05:59:00

CAMBRIDGE, Massachusetts, September 9, 2010 /PRNewswire-FirstCall/ -- Shire plc (LSE: SHP, NASDAQ: SHPGY), the global specialty biopharmaceutical company, today announced the expansion of its Human Genetic Therapies pipeline through the exclusive license, in markets outside of North America, for the activin receptor type IIB (ActRIIB) class of molecules being developed by Acceleron Pharma Inc., a private biotechnology company based in Cambridge, Massachusetts. The collaboration will...

2010-09-03 07:47:00

$11 Million Supports Five-Year Study to Compare Treatments ROCHESTER, N.Y., Sept. 3 /PRNewswire-USNewswire/ -- A large international study aimed at improving the care of muscular dystrophy patients worldwide is being launched by physicians, physical therapists, and researchers at the University of Rochester Medical Center. Neurologist Robert "Berch" Griggs, M.D., is heading the study of treatments for Duchenne muscular dystrophy, the most common form of the disease that affects children....

2010-08-31 00:33:00

AMSTERDAM, The Netherlands, August 31, 2010 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext: AMT), a leader in the field of human gene therapy, today reported its results for the first half year of 2010. Highlights - Glybera(R): - EMA initiated MAA review in 01/2010 - Approval progressing on schedule for decision mid 2011 - Novel biomarker for Glybera(R) activity identified - Hemophilia B: Phase I/II started - Duchenne Muscular...

2010-08-09 12:14:00

Dr. Jerry Mendell Leading Follistatin Gene Therapy MIDDLETOWN, Ohio, Aug. 9 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), will award a $600,000 grant to Nationwide Children's Hospital in Columbus, Ohio to conduct clinical testing of a promising gene therapy technique for muscle disease. (Logo:...

2010-08-02 15:00:00

NOVATO, Calif., Aug. 2 /PRNewswire-FirstCall/ -- BioMarin Pharmaceutical Inc. (Nasdaq: BMRN) announced today that it has completed the Phase 1 clinical study of BMN 195, a small molecule utrophin up-regulator, for the treatment of Duchenne muscular dystrophy (DMD). The Phase 1 clinical trial was a single-center, double-blind, placebo-controlled, single-dose escalation study followed by a multiple-dose escalation study in healthy volunteers. The administration of up to 400 mg/kg did not...

2010-07-14 09:55:00

Funds Will Help Offset Travel Costs for Participants MIDDLETOWN, Ohio, July 14 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that PPMD will provide a grant to clinical sites participating in Acceleron Pharma's Phase 2 clinical study of ACE-031. These grants will help patients'...

2010-06-22 05:00:00

SAN DIEGO, June 22 /PRNewswire-FirstCall/ -- LifeVantage Corporation (OTC Bulletin Board: LFVN), the maker of Protandim®, a patented, science-based solution to oxidative stress, announced today that a peer-reviewed manuscript was published in the Journal of Dietary Supplements examining the beneficial effects of Protandim® on a mouse model of Duchenne Muscular Dystrophy (DMD), an X-linked inherited disease affecting one in 3,500 males. Symptoms usually...

2010-06-18 09:30:00

Conference Includes Launch of First-Ever Duchenne Therapeutic Development Meeting MIDDLETOWN, Ohio, June 18 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that the Mayor of Denver, Colorado, John W. Hickenlooper, has proclaimed June 26, 2010 "End Duchenne Day" in recognition of...