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Latest Duchenne muscular dystrophy Stories

2011-05-19 00:00:00

AMSTERDAM, May 19, 2011 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext Amsterdam: AMT), a leader in the field of human gene therapy, today provides its non-audited business update in compliance with the EU transparency directive. This report summarizes material events and AMT's financial position for the first quarter of 2011. 1Q 2011 Highlights - Glybera(R): - Responses to Day 180 questions of the EMA/CHMP were submitted on schedule - EMA/CHMP...

2011-04-25 09:00:00

DETROIT, April 25, 2011 /PRNewswire/ -- Cadillac and Sony Music are auctioning a Justin Bieber prize package to benefit Cure Duchenne, a nonprofit group that funds research and awareness of Duchenne, the most common muscle disease in children. Fans can bid on a trip for two to see pop singer Bieber in concert at select locations on his world tour. The winner of the auction also will receive a copy of Bieber's new album, "Never Say Never - The Remixes," which features music from his...

2011-04-18 15:08:57

Researchers have long questioned why patients with Duchenne muscular dystrophy (DMD) tend to manage well through childhood and adolescence, yet succumb to their disease in early adulthood, or why elderly people who lose muscle strength following bed rest find it difficult or impossible to regain. Now, researchers at the National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS), part of the National Institutes of Health, are beginning to find answers in a specialized...

2011-04-04 11:04:00

Grant Funds Work of Ronald G. Victor, M.D. and Cedars-Sinai Medical Center HACKENSACK, N.J., April 4, 2011 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the largest, most comprehensive non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne) - announced today that they will award Ronald G. Victor, M.D. of Cedars-Sinai Medical Center, a $750,000 grant to fund his study of phosphodiesterase inhibitors...

2011-03-18 11:22:00

Zebrafish study highlights existing drugs that may help restore muscle in DMD BOSTON, March 18, 2011 /PRNewswire-USNewswire/ -- Armed with a zebrafish model of Duchenne muscular dystrophy (DMD) and a library of 1,200 chemicals already approved for human use, researchers at Children's Hospital Boston have identified a compound that reverses the loss of muscle structure and function associated with DMD, seemingly by compensating for the loss of a critical protein. The discovery, published...

2011-03-10 13:33:28

Mutation in important muscle protein causes muscle disease and cognitive impairment A strong international collaboration and a single patient with mild muscle disease and severe cognitive impairment have allowed University of Iowa researchers to identify a new gene mutation that causes muscular dystrophy. Furthermore, by engineering the human gene mutation into a mouse, the researchers, led by Kevin Campbell, Ph.D., professor and head of molecular physiology and biophysics at the UI Carver...

2011-03-06 23:59:00

AMSTERDAM, March 7, 2011 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (AMT) (Euronext: AMT), a leader in the field of human gene therapy, announced today that the Duchenne Parent Project, based in the Netherlands, has awarded AMT a grant of EUR 145,000 to support the development of AMT-080, AMT's gene therapy for Duchenne Muscular Dystrophy (DMD). DMD is a severe, fatal disease affecting young children, almost exclusively boys, characterized by progressive muscle...

2011-02-08 10:14:00

Efforts over decade result in $192 million in Duchenne-specific federal investment HACKENSACK, N.J., Feb. 8, 2011 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne) - will host their annual Advocacy Conference, including the One Voice Advocacy Summit, in Washington, D.C. from February 13 - 15, 2011. (Logo:...

2011-02-04 12:48:21

It's a gene called DOT1L, and if you don't have enough of the DOT1L enzyme, you could be at risk for some types of heart disease. These findings by UNC researchers appear in the Feb. 1, 2011 issue of the journal Genes and Development. Everyone knows chocolate is critical to a happy Valentine's Day. Now scientists are one step closer to knowing what makes a heart happy the rest of the year. It's a gene called DOT1L, and if you don't have enough of the DOT1L enzyme, you could be at risk for...

2011-02-01 12:00:00

SOUTH PLAINFIELD, N.J. and HACKENSACK, N.J., Feb. 1, 2011 /PRNewswire/ -- PTC Therapeutics, Inc. (PTC) and Parent Project Muscular Dystrophy (PPMD) today announced an expansion of their collaboration to discover new treatments for patients with Duchenne/Becker muscular dystrophy (DBMD). PPMD has awarded PTC a $250,000 grant, with the potential of additional funding, to advance drug discovery efforts in identifying a new treatment that improves heart function in patients with DBMD. (Logo:...


Word of the Day
cacodemon
  • An evil spirit; a devil.
  • A nightmare.
  • In astrology, the twelfth house of a scheme or figure of the heavens: so called from its signifying dreadful things, such as secret enemies, great losses, imprisonment, etc.
'Cacodemon' comes from a Greek term meaning 'evil genius.'
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