Quantcast
Last updated on April 18, 2014 at 13:00 EDT

Latest Duchenne muscular dystrophy Stories

2009-11-11 00:00:00

AMSTERDAM, November 11 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext: AMT), a leader in the field of human gene therapy, announced today that it has successfully treated Duchenne muscular dystrophy (DMD) in an animal model with its proprietary gene therapy. The proof of concept studies were performed in collaboration with the group of Professor Irene Bozzoni (University of Rome, La Sapienza, Italy) and demonstrated effectiveness in the heart as well as in skeletal...

2009-11-10 09:45:00

Using drugs to block the action of an enzyme called protein kinase C can reduce or even eliminate heart problems in mice with myotonic dystrophy, said researchers from Baylor College of Medicine in a report that appears Nov. 9 in the Journal of Clinical Investigation. "The disease is very severe in these mice," said Dr. Thomas Cooper, professor of pathology and molecular and cellular biology at BCM and senior author of the report. "Eighty percent of them die within three weeks of turning on...

2009-11-06 09:32:00

Dr. Carmen Bertoni to Receive $75,000 For Duchenne Muscular Dystrophy Research MIDDLETOWN, Ohio, Nov. 6 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced today the latest recipient of the End Duchenne Grant Award Program. Carmen Bertoni, Ph.D., Assistant Professor of the Department...

2009-10-20 09:28:53

New publication in Molecular Therapy outlines dramatic effects in animals treated with splice switching PPMO, demonstrates promise for treatment of Duchenne muscular dystrophy An exon skipping PPMO has demonstrated dramatic effects in the prevention and treatment of severely affected, dystrophin and utrophin-deficient mice, preventing severe deterioration of the treated animals and extending their lifespan. These findings were published online today in the journal Molecular Therapy and...

2009-10-16 10:26:00

DALLAS, Oct. 16 /PRNewswire-USNewswire/ -- John Killian, Chairman of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), and his wife Stefanie Killian, announced today that the 5th Annual Sam's Family Fun Day (Sam's Day) will take place on October 24, 2009 from 10am to 2pm on Flagpole Hill at White Rock Lake. (Photo: http://www.newscom.com/cgi-bin/prnh/20091016/DC93763)...

2009-10-13 00:00:00

AMSTERDAM, October 13 /PRNewswire-FirstCall/ -- Amsterdam Molecular Therapeutics (Euronext: AMT), a leader in the field of human gene therapy, announced today that the European Medicines Agency has granted Orphan Drug Designation to AMT's gene therapy product AMT-080 for the treatment of Duchenne muscular dystrophy. Orphan Drug Designation for Duchenne muscular dystrophy (DMD) entitles AMT to ten year market exclusivity in Europe following marketing approval for AMT-080 if this...

2009-09-29 06:00:00

Duchenne Organization Competes With Over 500 Nonprofits To Win Grand Prize MIDDLETOWN, Ohio, Sept. 29 /PRNewswire-USNewswire/ -- Intel, as Sponsors of Tomorrow(TM), announced Parent Project Muscular Dystrophy (PPMD) as the winner of its Vote For A Cause contest on its Facebook Page. Over 600 nonprofit organizations were nominated and based upon online voting by Facebook members, organizations were eliminated through five rounds of competition. PPMD is the recipient of $50,000 in...

2009-06-22 13:51:00

Senator Johnny Isakson, American Football Coaches Association to Receive Awards MIDDLETOWN, Ohio, June 22 /PRNewswire-USNewswire/ -- Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced that PPMD will be honoring United States Senator Johnny Isakson and the American Football Coaches Association (AFCA) with...

2009-06-18 12:36:10

British medical scientists say they used an animal study to demonstrate a method of making an early diagnosis of muscular dystrophy, before symptoms develop. University of Birmingham researchers said they used mice to study the key proteins involved in two types of muscular dystrophy -- Duchenne muscular dystrophy and a milder form, Limb Girdle MD. The researchers said they identified disrupted stem cell function and delays of skeletal muscle formation in embryos of muscular dystrophy-like...

2009-06-18 07:09:07

The saying "knowing is half the battle" is never more powerful than in early diagnosis and treatment of disease. Muscular dystrophy is one such disease where patients can benefit from early treatment. Researchers at the School of Biosciences, University of Birmingham, United Kingdom, used mice as models to study the key proteins involved in two types of muscular dystrophy (MD): the most severe MD form, Duchenne Muscular Dystrophy (DMD), and a milder form, Limb Girdle MD. The researchers found...