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Latest Duchenne muscular dystrophy Stories

2014-06-12 23:08:10

Central US location to serve as nationwide hub as MDA accelerates progress to find treatments and cures. Chicago, Illinois (PRWEB) June 12, 2014 The Muscular Dystrophy Association has a new national office from which to direct its mission, fundraising and operational strategies. The 64-year-old voluntary health agency announced today it has moved into its new national office in the city’s downtown business district. The office will serve as a hub for MDA’s executive management,...

2014-06-09 12:30:50

HACKENSACK, N.J., June 9, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the leading patient advocacy organization fighting to end Duchenne muscular dystrophy (Duchenne) - announced that a recent treatment preferences and benefit/risk study led by the organization has been published in Clinical Therapeutics. The article entitled, "A Community-Engaged Approach to Quantifying Caregiver Preferences for the Benefits and Risks of Emerging Therapies for Duchenne...

2014-05-23 08:23:53

- The first treatment for the underlying cause of Duchenne muscular dystrophy - SOUTH PLAINFIELD, N.J., May 23, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that following its request for re-examination, the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion regarding the company's application for a conditional marketing authorization of Translarna(TM) (ataluren) for the treatment...

Treating Deadly Duchenne Muscular Dystrophy With Viagra, Cialis
2014-05-08 13:35:59

Brett Smith for redOrbit.com - Your Universe Online Cialis and Viagra are typically prescribed to treat erectile dysfunction in men, but a new study has shown that these drugs could be used to treat a deadly disorder known as Duchenne muscular dystrophy (DMD). DMD is a genetic disorder in males marked by muscle weakness beginning in early childhood and quite often causing deformity of the forearms, legs and spine. Cardiovascular and respiratory muscles usually begin to decline when...

2014-04-21 16:25:21

Urges FDA to Move Quickly with Final Approval of Eteplirsen WASHINGTON, April 21, 2014 /PRNewswire/ -- The Race to Yes campaign today lauded drug maker Sarepta on its plans to move forward immediately to seek FDA approval of the first drug to successfully treat Duchenne muscular dystrophy, the world's leading genetic killer of children. http://photos.prnewswire.com/prnvar/20140311/MM81272LOGO "We have been waiting for this for a long time," said Tracy Seckler, whose son, Charley,...

2014-04-09 12:31:44

WASHINGTON, April 9, 2014 /PRNewswire-iReach/ -- Parents of children facing death from Duchenne muscular dystrophy today asked the U.S. Food and Drug Administration to approve in 30 days a well-tested drug that halts the disease with no side effects. (Photo: http://photos.prnewswire.com/prnh/20140409/MN00963) The parents, representing The Race to Yes campaign, challenged FDA Commissioner Margaret Hamburg to take the steps needed to approve the drug - eteplirsen - following positive comments...

2014-03-26 08:29:20

Urges President to Support Safe and Effective Treatment for Duchenne Muscular Dystrophy WASHINGTON, March 26, 2014 /PRNewswire/ -- The Race to Yes, a national campaign by families with children facing death from Duchenne Muscular Dystrophy achieved an important milestone just after 8pm EDT last night when the 100,000th person signed their White House petition urging the U.S. Food and Drug Administration to approve a breakthrough drug that has been shown to halt the progress of the...

2014-03-21 23:01:12

The John Owen Adventure Dodgeball event is for children and adults alike to raise money and awareness for the fatal disease, Duchenne Muscular Dystrophy. North Royalton, OH (PRWEB) March 21, 2014 John Owen's Adventure Inc. is thrilled to launch the second annual Play for JOA-Dodgeball event bringing together children and adults alike to enjoy this classic sport while fundraising to cure the fatal disease Duchenne Muscular Dystrophy (DMD). "Our 2013 Tourney was a huge...

2014-03-20 16:26:23

Leading Duchenne Organization Launches Certified Duchenne Care Center Program HACKENSACK, N.J., March 20, 2014 /PRNewswire-USNewswire/ -- Nationwide Children's Hospital was named the first Certified Duchenne Care Center by Parent Project Muscular Dystrophy (PPMD), the leading advocacy organization working to end Duchenne muscular dystrophy (Duchenne). PPMD is launching the Certified Duchenne Care Center Program as part of its robust Transforming Duchenne Care Initiative. Over the...

2014-03-14 08:27:16

CAMBRIDGE, Mass., March 14, 2014 /PRNewswire/ -- Catabasis Pharmaceuticals Inc. today announced that data from its Phase 1 clinical trial of SMART Linker conjugate CAT-1004 will be presented at the Muscular Dystrophy Association's 2014 Clinical Conference in Chicago, Ill. Catabasis' chief medical officer, Joanne Donovan, M.D., Ph.D., will discuss Duchenne muscular dystrophy (DMD) animal model data and data from a Phase 1 clinical trial during the poster session from 6:00 to 8:00 p.m. CDT on...


Word of the Day
endocarp
  • The hard inner (usually woody) layer of the pericarp of some fruits (as peaches or plums or cherries or olives) that contains the seed.
This word comes from the Greek 'endon,' in, within, plus the Greek 'karpos', fruit.
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