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Latest Duchenne muscular dystrophy Stories

2014-07-08 12:28:25

THE LABOR DAY WEEKEND TRADITION WILL AIR IN PRIMETIME, SUNDAY, AUGUST 31, 9|8C CHICAGO, July 8, 2014 /PRNewswire/ -- For the first time, the Muscular Dystrophy Association's nationally broadcast telethon the MDA Show of Strength Telethon, one of America's longest-standing and beloved fundraising and entertainment events, will invite America to help shape the content of the show to air this Labor Day weekend. http://photos.prnewswire.com/prnvar/20140708/124950 "For decades,...

2014-06-30 08:30:29

SOUTH PLAINFIELD, N.J., June 30, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that it is the recipient of Parent Project Muscular Dystrophy's (PPMD) "Path to Progress" award, honoring PTC's 16 years of commitment to bring the first-ever therapy for the underlying cause of the disorder to patients with Duchenne muscular dystrophy (DMD). The award was presented at PPMD's Annual Connect Conference in Chicago, Illinois....

2014-06-25 12:30:09

Parent Project Muscular Dystrophy-led guidance seeks to address unmet clinical needs of individuals with Duchenne muscular dystrophy and accelerate development of safe and effective therapies CHICAGO, June 25, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) and a broad coalition of stakeholders today submitted the first-ever patient advocacy-initiated draft guidance for a rare disease to the U.S. Food and Drug Administration (FDA) to help accelerate development and...

2014-06-23 16:24:42

Leading Duchenne-specific Organization Marks Anniversary with Largest International Meeting to Date HACKENSACK, N.J., June 23, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the leading advocacy organization working to end Duchenne muscular dystrophy (Duchenne) will hold their 20(th) Annual Connect Conference in Chicago, Illinois, June 26-29, 2014. The State of Illinois will recognize the event by declaring the week of June 23 as Duchenne Muscular Dystrophy...

2014-06-12 23:08:10

Central US location to serve as nationwide hub as MDA accelerates progress to find treatments and cures. Chicago, Illinois (PRWEB) June 12, 2014 The Muscular Dystrophy Association has a new national office from which to direct its mission, fundraising and operational strategies. The 64-year-old voluntary health agency announced today it has moved into its new national office in the city’s downtown business district. The office will serve as a hub for MDA’s executive management,...

2014-06-09 12:30:50

HACKENSACK, N.J., June 9, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the leading patient advocacy organization fighting to end Duchenne muscular dystrophy (Duchenne) - announced that a recent treatment preferences and benefit/risk study led by the organization has been published in Clinical Therapeutics. The article entitled, "A Community-Engaged Approach to Quantifying Caregiver Preferences for the Benefits and Risks of Emerging Therapies for Duchenne...

2014-05-23 08:23:53

- The first treatment for the underlying cause of Duchenne muscular dystrophy - SOUTH PLAINFIELD, N.J., May 23, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that following its request for re-examination, the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion regarding the company's application for a conditional marketing authorization of Translarna(TM) (ataluren) for the treatment...

Treating Deadly Duchenne Muscular Dystrophy With Viagra, Cialis
2014-05-08 13:35:59

Brett Smith for redOrbit.com - Your Universe Online Cialis and Viagra are typically prescribed to treat erectile dysfunction in men, but a new study has shown that these drugs could be used to treat a deadly disorder known as Duchenne muscular dystrophy (DMD). DMD is a genetic disorder in males marked by muscle weakness beginning in early childhood and quite often causing deformity of the forearms, legs and spine. Cardiovascular and respiratory muscles usually begin to decline when...

2014-04-21 16:25:21

Urges FDA to Move Quickly with Final Approval of Eteplirsen WASHINGTON, April 21, 2014 /PRNewswire/ -- The Race to Yes campaign today lauded drug maker Sarepta on its plans to move forward immediately to seek FDA approval of the first drug to successfully treat Duchenne muscular dystrophy, the world's leading genetic killer of children. http://photos.prnewswire.com/prnvar/20140311/MM81272LOGO "We have been waiting for this for a long time," said Tracy Seckler, whose son, Charley,...

2014-04-09 12:31:44

WASHINGTON, April 9, 2014 /PRNewswire-iReach/ -- Parents of children facing death from Duchenne muscular dystrophy today asked the U.S. Food and Drug Administration to approve in 30 days a well-tested drug that halts the disease with no side effects. (Photo: http://photos.prnewswire.com/prnh/20140409/MN00963) The parents, representing The Race to Yes campaign, challenged FDA Commissioner Margaret Hamburg to take the steps needed to approve the drug - eteplirsen - following positive comments...


Word of the Day
jument
  • A beast of burden; also, a beast in general.
'Jument' ultimately comes from the Latin 'jugum,' yoke.
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