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Latest Duchenne muscular dystrophy Stories

2014-07-11 08:24:34

PPMD one of four patient organizations testifying on 21st Century Cures Initiative; Focus will be on Accelerating Access Initiative HACKENSACK, N.J., July 11, 2014 /PRNewswire-USNewswire/ -- Pat Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the leading advocacy organization working to end Duchenne muscular dystrophy (Duchenne), will testify today before a key Congressional committee focused on accelerating development and delivery of therapies to patients....

2014-07-09 16:28:13

-French ATU Cohort and Other Named Patient Programs Authorized - SOUTH PLAINFIELD, N.J., July 9, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced the initiation of a reimbursed expanded access program (EAP). PTC's EAP program is intended to make Translarna(TM) (ataluren) available to patients before commercial availability in certain countries. Where mechanisms exist and in accordance with local regulations, PTC will make Translarna available to nonsense...

2014-07-08 12:28:25

THE LABOR DAY WEEKEND TRADITION WILL AIR IN PRIMETIME, SUNDAY, AUGUST 31, 9|8C CHICAGO, July 8, 2014 /PRNewswire/ -- For the first time, the Muscular Dystrophy Association's nationally broadcast telethon the MDA Show of Strength Telethon, one of America's longest-standing and beloved fundraising and entertainment events, will invite America to help shape the content of the show to air this Labor Day weekend. http://photos.prnewswire.com/prnvar/20140708/124950 "For decades,...

2014-06-30 08:30:29

SOUTH PLAINFIELD, N.J., June 30, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that it is the recipient of Parent Project Muscular Dystrophy's (PPMD) "Path to Progress" award, honoring PTC's 16 years of commitment to bring the first-ever therapy for the underlying cause of the disorder to patients with Duchenne muscular dystrophy (DMD). The award was presented at PPMD's Annual Connect Conference in Chicago, Illinois....

2014-06-25 12:30:09

Parent Project Muscular Dystrophy-led guidance seeks to address unmet clinical needs of individuals with Duchenne muscular dystrophy and accelerate development of safe and effective therapies CHICAGO, June 25, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) and a broad coalition of stakeholders today submitted the first-ever patient advocacy-initiated draft guidance for a rare disease to the U.S. Food and Drug Administration (FDA) to help accelerate development and...

2014-06-23 16:24:42

Leading Duchenne-specific Organization Marks Anniversary with Largest International Meeting to Date HACKENSACK, N.J., June 23, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the leading advocacy organization working to end Duchenne muscular dystrophy (Duchenne) will hold their 20(th) Annual Connect Conference in Chicago, Illinois, June 26-29, 2014. The State of Illinois will recognize the event by declaring the week of June 23 as Duchenne Muscular Dystrophy...

2014-06-12 23:08:10

Central US location to serve as nationwide hub as MDA accelerates progress to find treatments and cures. Chicago, Illinois (PRWEB) June 12, 2014 The Muscular Dystrophy Association has a new national office from which to direct its mission, fundraising and operational strategies. The 64-year-old voluntary health agency announced today it has moved into its new national office in the city’s downtown business district. The office will serve as a hub for MDA’s executive management,...

2014-06-09 12:30:50

HACKENSACK, N.J., June 9, 2014 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) - the leading patient advocacy organization fighting to end Duchenne muscular dystrophy (Duchenne) - announced that a recent treatment preferences and benefit/risk study led by the organization has been published in Clinical Therapeutics. The article entitled, "A Community-Engaged Approach to Quantifying Caregiver Preferences for the Benefits and Risks of Emerging Therapies for Duchenne...

2014-05-23 08:23:53

- The first treatment for the underlying cause of Duchenne muscular dystrophy - SOUTH PLAINFIELD, N.J., May 23, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that following its request for re-examination, the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion regarding the company's application for a conditional marketing authorization of Translarna(TM) (ataluren) for the treatment...

Treating Deadly Duchenne Muscular Dystrophy With Viagra, Cialis
2014-05-08 13:35:59

Brett Smith for redOrbit.com - Your Universe Online Cialis and Viagra are typically prescribed to treat erectile dysfunction in men, but a new study has shown that these drugs could be used to treat a deadly disorder known as Duchenne muscular dystrophy (DMD). DMD is a genetic disorder in males marked by muscle weakness beginning in early childhood and quite often causing deformity of the forearms, legs and spine. Cardiovascular and respiratory muscles usually begin to decline when...


Word of the Day
conjunto
  • A style of popular dance music originating along the border between Texas and Mexico, characterized by the use of accordion, drums, and 12-string bass guitar and traditionally based on polka, waltz, and bolero rhythms.
The word 'conjunto' comes through Spanish, from Latin coniūnctus, past participle of coniungere, to join together; see conjoin