Latest enzyme replacement therapy Stories
Novel ZFN Genome Editing Approach Results in Sustained Levels of Enzymes Associated with Hunter, Hurler and Gaucher Syndromes RICHMOND, Calif., Feb.
Former head of rare diseases at Genzyme brings a 20-year track record of delivering successful, innovative products to patients throughout the world PHILADELPHIA, Dec.
- MPS IV A patients and families urge swift, publicly funded access to life-altering drug VIMIZIM(TM) - VANCOUVER, July 7, 2014 /CNW/ - The Canadian Society for Mucopolysaccharide
What causes brain damage and inflammation in severe cases of Gaucher disease?
A genetic condition that attacks multiple organs and usually results in fatal heart problems can be detected using a new MRI technique that was developed at the University of Alberta.