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Latest Gene therapy Stories

2014-06-16 08:29:08

Company will draw on leaders' expertise in rare diseases, R&D and commercialization as it moves to complete development of its lead program in inherited blindness PHILADELPHIA, June 16, 2014 /PRNewswire/ -- Spark Therapeutics, a late-stage gene therapy company developing treatments for a wide range of rare, debilitating diseases, announced today the appointments of Lars Ekman, former president of research and development at Elan, and Vin Milano, former president and CEO of...

2014-06-12 12:26:31

Lack of Disease-Modifying Therapies is Expected to Remain a Critical Unmet Need and Provides Ample Opportunity for Developers, According to Findings from Decision Resources Group BURLINGTON, Mass., June 12, 2014 /PRNewswire/ -- Decision Resources Group finds that three therapies, Teva's Huntexil, Auspex's SD-809 and Raptor's Procysbi, will likely receive regulatory approval for Huntington's disease (HD) in the United States and the EU5 markets (Germany, France, Italy, Spain and United...

2014-06-12 08:30:19

SAN DIEGO, June 12, 2014 /PRNewswire/ -- Taxus Cardium Pharmaceuticals Group Inc. (Trading Symbol: CRXM), announced today that Cardium Therapeutics will announce interim results on the Generx(®) angiogenic gene therapy product candidate international ASPIRE Phase 3 registration study at the 2014 BIO International Convention. Hosted by the Biotechnology Industry Organization (BIO), this year's global event for biotechnology will take place June 23-26 at the San Diego Convention Center...

2014-06-10 12:32:05

Internationally recognized physician-scientists joining fight against devastating childhood diseases as hospital expands clinical and basic science research MEMPHIS, Tenn., June 10, 2014 /PRNewswire-USNewswire/ -- St. Jude Children's Research Hospital officials today announced the appointment of three internationally recognized physician-scientists to leadership positions. Mitchell Weiss, M.D., Ph.D., has been named chair of the St. Jude Department of Hematology. He was recruited...

2014-06-05 23:01:58

Barbara and Edward Netter awarded prestigious distinction by the American Society of Gene and Cell Therapy. Washington, DC (PRWEB) June 05, 2014 Barbara Netter and her late husband Edward Netter – Greenwich residents and founders of Alliance for Cancer Gene Therapy (ACGT) – were awarded the prestigious Distinguished Service Award by the American Society of Gene and Cell Therapy (ASGCT) on Thursday, May 22, 2014. The award – presented in Washington, DC before an audience of over...

2014-06-03 23:03:40

Eighth-annual Greenwich-Stamford Open Water Swim unites Connecticut residents in the fight against cancer. Stamford, CT (PRWEB) June 03, 2014 Across Connecticut, residents intent on conquering cancer are preparing to swim the Long Island Sound to raise funds, bolster awareness and seek out a cure at the eighth-annual Greenwich-Stamford Swim Across America (SAA) benefiting the Alliance for Cancer Gene Therapy (ACGT). On Saturday, June 21, hundreds of swimmers and philanthropists will unite...

2014-06-02 16:25:27

PHILADELPHIA, June 2, 2014 /PRNewswire/ -- Spark Therapeutics, Inc., a late-stage gene therapy company developing treatments for a wide range of rare, debilitating diseases, announced today that company leadership will present at three healthcare investor meetings in June. -- 2014 Jefferies Global Healthcare Conference, New York City, June 5 Jeffrey D. Marrazzo, co-founder and CEO of Spark, will present on Spark's leadership in the advancement of potentially curative,...

2014-05-28 16:26:41

Groundbreaking Nature Publication Describes Successful ZFN Driven Genome Editing in Long-Term Repopulating Stem Cells Necessary for Clinical Translation RICHMOND, Calif., May 28, 2014 /PRNewswire/ -- Sangamo BioSciences, Inc. (Nasdaq: SGMO) announced today the publication in Nature of data demonstrating efficient zinc finger nuclease (ZFN)-mediated, targeted gene insertion that resulted in correction of the genetic defect in stem cells from an individual with X-linked severe combined...

2014-05-27 16:25:11

Gene therapy leader to advance its deep pipeline of rare disease programs including its lead Phase 3 product candidate for RPE65-related blindness PHILADELPHIA, May 27, 2014 /PRNewswire/ -- Spark Therapeutics, a late-stage company developing gene-based medicines for a wide range of rare, debilitating diseases, today announced the successful completion of a $72.8 million Series B financing led by Sofinnova Ventures. Joining Sofinnova as new investors in the company are Brookside...

2014-05-27 15:22:17

Aarhus University Aarhus University has developed a technology that uses the HIV virus as a tool in the fight against hereditary diseases For the first time researchers have succeeded in altering HIV virus particles so that they can simultaneously, as it were, 'cut and paste' in our genome via biological processes. Developed at the Department of Biomedicine at Aarhus University, the technology makes it possible to repair genomes in a new way. It also offers good perspectives for...


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bibliopole
  • A bookseller; now, especially, a dealer in rare and curious books.
This word comes from a Greek phrase meaning 'book seller.'
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