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Latest Gene therapy Stories

2014-02-11 08:32:36

Company continues to expand its board and leadership team as it moves toward completion of its Phase 3 gene therapy program and advancement of the industry's deepest pipeline of gene-based medicines PHILADELPHIA, Feb. 11, 2014 /PRNewswire/ -- Spark Therapeutics, a late-stage company developing gene-based medicines for a wide range of debilitating diseases, announced today the appointment of Elliott Sigal, M.D., Ph.D., former director, executive vice president and chief scientific officer of...

2014-02-10 20:21:08

Call on FDA for Accelerated Approval of Promising Duchenne Muscular Dystrophy Treatment WASHINGTON, Feb. 10, 2014 /PRNewswire-iReach/ -- Health staffers from over 80 Congressional offices together with agency and industry officials jammed a briefing room last Friday to hear mothers, clinicians and leading researchers call on the FDA to accept and promptly review a new drug application for eteplirsen, a promising new treatment for Duchenne Muscular Dystrophy that could save thousands...

2014-02-04 12:28:02

CINCINNATI, Feb. 4, 2014 /PRNewswire-USNewswire/ -- Researchers used blood platelets and bone marrow cells to deliver potentially curative gene therapy to mouse models of the human genetic disorder Hurler syndrome - an often fatal condition that causes organ damage and other medical complications. (Logo: http://photos.prnewswire.com/prnh/20110406/MM79025LOGO) Scientists from Cincinnati Children's Hospital Medical Center and the National Institute of Neurological Disorders and...

2014-02-04 08:36:15

CLEVELAND, Feb. 4, 2014 /PRNewswire-USNewswire/ -- Juventas Therapeutics, a privately-held, clinical-stage company developing novel regenerative therapies for the treatment of cardiovascular disease, announced today that it has initiated enrollment of the Phase II RETRO-HF clinical trial to evaluate safety and efficacy of JVS-100 delivered via retrograde infusion to patients with symptomatic heart failure. Co-principal investigators for the trial are Drs. Amit Patel, M.D., Director...

Precise Gene Modification In Monkeys Paves Way For Valuable Human Disease Models
2014-01-30 15:58:45

Cell Press Monkeys are important for modeling diseases because of their close similarities to humans, but past efforts to precisely modify genes in primates have failed. In a study published by Cell Press January 30th in the journal Cell, researchers achieved precise gene modification in monkeys for the first time using an efficient and reliable approach known as the CRISPR/Cas9 system. The study opens promising new avenues for the development of more effective treatments for a range of...

2014-01-29 20:23:48

DUBLIN, January 30, 2014 /PRNewswire/ -- Research and Markets ( http://www.researchandmarkets.com/research/jm2ns9/personalized) has announced the addition of a new report "Personalized Medicine - Scientific and Commercial Aspects" [http://www.researchandmarkets.com/research/jm2ns9/personalized ] to their offering. (Logo: http://photos.prnewswire.com/prnh/20130307/600769 ) The aim of personalized medicine or individualized treatment is to match the right drug to...

2014-01-28 20:22:25

DUBLIN, Ireland, January 28, 2014 /PRNewswire/ -- Research and Markets ( http://www.researchandmarkets.com/research/fvxjv3/cardiovascular) has announced the addition of a new report "Global Cardiovascular Drug Delivery Market" [http://www.researchandmarkets.com/research/fvxjv3/cardiovascular ] to their offering. (Logo: http://photos.prnewswire.com/prnh/20130307/600769 ) Drug delivery to the cardiovascular system is different from delivery to other systems because...

2014-01-21 23:00:06

Concierge doctor releases new book on stem cell research and anti-aging medicine. TAMPA, Fla. (PRWEB) January 22, 2014 Society’s continual, obsessive search for perpetual youth has lead many on a tumultuous path of medical mayhem from shots to creams and a variety of procedures in between. A leader in modern medicine, Dr. Burton Feinerman has always been at the forefront of new and life changing procedures in the healthcare community. Feinerman's experience includes his time as a...

2014-01-16 16:23:39

DUBLIN, January 16, 2014 /PRNewswire/ -- Research and Markets ( http://www.researchandmarkets.com/research/pcgfhj/cell_therapy) has announced the addition of a new report "Global Cell Therapy - Technologies, Markets and Companies" [http://www.researchandmarkets.com/research/pcgfhj/cell_therapy ] to their offering. (Logo: http://photos.prnewswire.com/prnh/20130307/600769 ) This report describes and evaluates cell therapy technologies and methods, which have...

Eye Gene Therapy
2014-01-16 09:44:41

Brett Smith for redOrbit.com - Your Universe Online A newly developed genetic therapy for treating a type of inherited blindness called choroideremia is showing some promise and allowing patients to see incrementally more than they had before the treatment, according to a new report in The Lancet. Six patients in the study had one eye treated with the gene therapy in operations at the Oxford Eye Hospital in the United Kingdom. After six months, the treated eye showed improved vision in...


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  • Boughs or branches.
  • Warbling of birds in trees.
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