Latest Lysosomal storage disease Stories
Data from Disease Models of Hunter and Hurler Syndromes Demonstrate Proof of Concept for Sangamo's In Vivo Protein Replacement Platform RICHMOND, Calif., May 18, 2015 /PRNewswire/
CALABASAS, Calif., April 8, 2015 /PRNewswire/ -- ArmaGen, Inc., a privately held biotechnology company focused on developing novel therapies to treat severe neurological disorders, announced
SOUTH PLAINFIELD, N.J., March 19, 2015 /PRNewswire/ -- PTC Therapeutics, Inc.
Novel ZFN Genome Editing Approach Results in Sustained Levels of Enzymes Associated with Hunter, Hurler and Gaucher Syndromes RICHMOND, Calif., Feb.
LEXINGTON, Mass., Feb.
CALABASAS, Calif., Dec.
Data Demonstrate Therapeutic Levels of Clotting Factor for Hemophilia in Non-Human Primates and In Vivo Protein Production of Lysosomal Storage Disease Enzymes RICHMOND, Calif., Dec.
HARRISBURG, Pa., Oct.
- An uxorious, effeminate, or spiritless man.
- A timorous, cowardly fellow.