Latest Lysosomal storage disease Stories
SOUTH PLAINFIELD, N.J., March 19, 2015 /PRNewswire/ -- PTC Therapeutics, Inc.
Novel ZFN Genome Editing Approach Results in Sustained Levels of Enzymes Associated with Hunter, Hurler and Gaucher Syndromes RICHMOND, Calif., Feb.
LEXINGTON, Mass., Feb.
CALABASAS, Calif., Dec.
Data Demonstrate Therapeutic Levels of Clotting Factor for Hemophilia in Non-Human Primates and In Vivo Protein Production of Lysosomal Storage Disease Enzymes RICHMOND, Calif., Dec.
HARRISBURG, Pa., Oct.
- Large; stout; burly.