Latest muscular dystrophy Stories
Stem cells from patients with a rare form of muscular dystrophy have been successfully transplanted into mice affected by the same form of dystrophy, according to a new study published today in Science Translational Medicine. For the first time, scientists have turned muscular dystrophy patients' fibroblast cells (common cells found in connective tissue) into stem cells and then differentiated them into muscle precursor cells. The muscle cells were then genetically modified and...
SOUTH PLAINFIELD, N.J., June 27, 2012 /PRNewswire/ -- PTC Therapeutics, Inc. (PTC) today announced the initiation of an open-label study in the European Union, Israel, Australia and Canada for patients with nonsense mutation Duchenne/Becker muscular dystrophy (nmDBMD) who received ataluren in a prior, PTC-sponsored clinical study. The primary objective of this study is to gain further information on the long-term safety and tolerability of ataluren, an investigational new drug. PTC...
CINCINNATI, June 26, 2012 /PRNewswire-USNewswire/ -- The first landmark randomized clinical trial for a cardiac drug regimen in Duchenne muscular dystrophy (DMD) is testing whether earlier treatment can stop or slow down heart damage that usually kills people with the disease. (Logo: http://photos.prnewswire.com/prnh/20110406/MM79025LOGO) The study is a collaboration of Cincinnati Children's Hospital Medical Center, Ohio State University (OSU) and The Christ Hospital in...
Meeting to Take Place at Annual Connect Conference in Ft. Lauderdale HACKENSACK, N.J., June 25, 2012 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD) will host the first Transforming Duchenne Care Meeting, June 27-28, 2012, immediately preceding the Annual Connect Conference in Fort Lauderdale, Florida. The goal of the Transforming Duchenne Care Meeting is to bring together leadership from top medical institutions, neuromuscular experts, and patient...
'A Molecular Bandage for Diseased Muscle' appears today in prestigious Science publication Leading muscular dystrophy researcher Dean Burkin, of the University of Nevada School of Medicine summarizes the impact of a new protein therapeutic, MG53, for the treatment of Duchenne muscular dystrophy in an article published this week in Science Translational Medicine. "This is a focus article in which we summarize the impact of MG53 protein therapy as a treatment option and discuss the...
HACKENSACK, N.J., June 20, 2012 /PRNewswire-USNewswire/ -- AVI BioPharma is teaming up with Parent Project Muscular Dystrophy (PPMD)'s endurance program, Run For Our Sons, to participate in the Rock 'n' Roll Seattle Marathon & Half Marathon on June 23, 2012. The goal is to raise money and awareness to help end Duchenne muscular dystrophy (Duchenne), the most common form of muscular dystrophy. (Logo: http://photos.prnewswire.com/prnh/20100119/DC39975LOGO) AVI and PPMD have a...
Letter Signed by Nearly 120 Organizations, Latest PDUFA-Oriented Action HACKENSACK, N.J., June 13, 2012 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), the nation's largest Duchenne muscular dystrophy (Duchenne) advocacy organization - co-led a letter to key lawmakers that was signed by 119 organizations and that urges Congress to include the strongest patient engagement and rare disease provisions within the final use fee legislation. (Logo:...
Volunteers Still Needed in Many States TUCSON, Ariz., June 5, 2012 /PRNewswire-USNewswire/ -- The Muscular Dystrophy Association has announced that more than 4,100 youngsters with muscular dystrophy and related muscle diseases will attend weeklong MDA summer camp sessions between now and late-August. (Logo: http://photos.prnewswire.com/prnh/20120424/DC93207LOGO) "MDA summer camp is the highlight of the summer for thousands of children with neuromuscular diseases across the...
"Muscle atrophy is a major problem with arthritis is now being treated at he Center for regenerative Medicine," according to A.J. Farshchian MD from the Center for Regenerative Medicine. Miami, FL (PRWEB) May 26, 2012 Muscle atrophy a major problem with arthritis, could be treated with regenerative medicine, according to A.J. Farshchian MD from the Center for Regenerative Medicine. Muscle atrophy also known as Muscle wasting Is common in arthritis and is usually due to loss of...
HACKENSACK, N.J., May 24, 2012 /PRNewswire-USNewswire/ -- As the U.S. Senate continues debate on legislation that seeks to accelerate delivery of safe and effective therapies to patients and to increase the patient voice as part of the therapy review process, Parent Project Muscular Dystrophy (PPMD) is pleased to offer its enthusiastic endorsement of the legislation. (Logo: http://photos.prnewswire.com/prnh/20100119/DC39975LOGO) Over the past several months, PPMD - the leading...
