Latest Rare diseases Stories
EPI-743 in phase 2B development for Leigh syndrome MOUNTAIN VIEW, Calif., June 9, 2014 /PRNewswire/ -- Edison Pharmaceuticals today announced that the FDA has granted Orphan Drug status
New officers focused on uniting the multiple system atrophy community to defeat the rare and terminal, neurodegenerative disorder.
WASHINGTON, June 4, 2014 /PRNewswire-USNewswire/ -- In a letter submitted today to the U.S.
LEXINGTON, Mass., June 3, 2014 /PRNewswire/ -- Synageva BioPharma Corp. (Synageva) (NASDAQ: GEVA), a biopharmaceutical company
Staff expanded in preparation for initiation of pulmonary and ophthalmic clinical trials DURHAM, N.C., June 2, 2014 /PRNewswire/ -- Parion Sciences, a company dedicated to the development of
Couple Builds upon Success of Last Year’s Event to Raise Awareness of Little-Known Disease at Lakeside Michigan Event Gull Lake, MI (PRWEB) May 29, 2014
Focused Rowing Efforts & New Film Support Crucial ALS Research CHONSHOHOKEN, Pa., May 20, 2014 /PRNewswire/ -- For the next six months, Philadelphia will play host to another revolution,
- Data Demonstrate Positive Trends in Lung Function and Pulmonary Exacerbations - SOUTH PLAINFIELD, N.J., May 16, 2014 /PRNewswire/ -- PTC Therapeutics, Inc.
TORONTO, May 15, 2014 /CNW/ - The month of May is tuberous sclerosis complex (TSC) awareness month in Canada, and May 15(th) is TSC Global Awareness Day.
Research initiative focused on developing improved treatments for tuberous sclerosis complex patients brings hope on TSC Awareness Day GRAND RAPIDS, Mich., May 15, 2014 /PRNewswire/
- Having no light.