Latest Rare diseases Stories
Para-equestrian champion Rebecca Hart proves that having a disability doesn't derail your dreams. UNIONVILLE, Pa., June 17, 2014 /PRNewswire/ -- Born with a very rare genetic condition
Uniquely Positioned to Provide Big Data Analytics for Over 6,800 Rare Diseases BRANFORD, Conn., June 11, 2014 /PRNewswire/ -- BioXcel Corporation, announced today its first-in-class
EPI-743 in phase 2B development for Leigh syndrome MOUNTAIN VIEW, Calif., June 9, 2014 /PRNewswire/ -- Edison Pharmaceuticals today announced that the FDA has granted Orphan Drug status
New officers focused on uniting the multiple system atrophy community to defeat the rare and terminal, neurodegenerative disorder.
WASHINGTON, June 4, 2014 /PRNewswire-USNewswire/ -- In a letter submitted today to the U.S.
LEXINGTON, Mass., June 3, 2014 /PRNewswire/ -- Synageva BioPharma Corp. (Synageva) (NASDAQ: GEVA), a biopharmaceutical company
Staff expanded in preparation for initiation of pulmonary and ophthalmic clinical trials DURHAM, N.C., June 2, 2014 /PRNewswire/ -- Parion Sciences, a company dedicated to the development of
Couple Builds upon Success of Last Year’s Event to Raise Awareness of Little-Known Disease at Lakeside Michigan Event Gull Lake, MI (PRWEB) May 29, 2014
Focused Rowing Efforts & New Film Support Crucial ALS Research CHONSHOHOKEN, Pa., May 20, 2014 /PRNewswire/ -- For the next six months, Philadelphia will play host to another revolution,
- Data Demonstrate Positive Trends in Lung Function and Pulmonary Exacerbations - SOUTH PLAINFIELD, N.J., May 16, 2014 /PRNewswire/ -- PTC Therapeutics, Inc.
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