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Last updated on April 19, 2014 at 5:20 EDT

Latest Spinal muscular atrophy Stories

2013-09-19 08:28:04

Improvements in muscle function continue to be observed up to fourteen months after a single dose CARLSBAD, Calif., Sept. 19, 2013 /PRNewswire/ -- Isis Pharmaceuticals, Inc. (NASDAQ: ISIS) announced today that follow-up preliminary data from a single dose, open-label Phase 1 study of ISIS-SMN(Rx) in children with spinal muscular atrophy (SMA), show that most SMA children receiving the two highest doses of the drug (6 mg and 9 mg) continued to show improvements in muscle function...

2013-09-09 08:26:40

--Biogen Idec and Isis to leverage antisense technology to accelerate discovery and development of novel therapies-- WESTON, Mass. and CARLSBAD, Calif., Sept. 9, 2013 /PRNewswire/ -- Biogen Idec (NASDAQ: BIIB) and Isis Pharmaceuticals, Inc. (NASDAQ: ISIS) today announced that the companies have entered into a broad, multi-year collaboration to leverage antisense technology to advance the treatment of neurological diseases. The agreement combines Biogen Idec's expertise in neurology with Isis'...

2013-08-29 23:18:59

Teen pop sensation makes his first national television appearance since taking home the 2013 "Artist to Watch" award at the 2013 MTV Video Music Awards. Tucson, Ariz. (PRWEB) August 29, 2013 Teen pop sensation Austin Mahone will make his first national television appearance since taking home the 2013 "Artist to Watch" award at the 2013 MTV Video Music Awards with a special performance on the 48th annual MDA Show of Strength Telethon, Sunday, Sept. 1, 9/8c, on ABC...

2013-08-28 23:19:10

Two-time Emmy Award winner, Grammy Award winner, and multi-platinum recording artist Paula Abdul will make her second consecutive appearance on the MDA Show of Strength Telethon. Tucson, Ariz., (PRWEB) August 28, 2013 Two-time Emmy Award winner, Grammy Award winner, and multi-platinum recording artist Paula Abdul will make her second consecutive appearance on the MDA Show of Strength Telethon Labor Day weekend, Sunday, Sept. 1, 9/8c, on ABC television stations across the country. Abdul,...

2013-08-26 23:17:31

Platinum-selling country star will perform his summer anthem and current single "Radio" on the 48th annual national broadcast. Tucson, AZ (PRWEB) August 26, 2013 Platinum-selling country star Darius Rucker will perform his summer anthem and current single "Radio" from his new album True Believers on the 48th annual national broadcast of the MDA Show of Strength Telethon on Labor Day weekend, Sunday, Sept. 1, 9/8c, on ABC television stations across the country....

2013-08-13 08:28:00

Ryan Seacrest, Luke Bryan, Backstreet Boys, Darius Rucker, Paula Abdul, Enrique Iglesias, Matthew Morrison and Austin Mahone among those to appear on two-hour broadcast TUCSON, Ariz., Aug. 13, 2013 /PRNewswire-USNewswire/ -- The Muscular Dystrophy Association has announced a star-studded celebrity lineup that will appear on its 48th annual telethon this Labor Day weekend, Sunday, Sept. 1, 9/8c, on ABC television stations across the country. (Logo:...

2013-08-09 23:03:53

Families of SMA is dedicated to creating a treatment and cure for Spinal Muscular Atrophy by funding and advancing a comprehensive research program, including drug discovery programs to make practical new therapies. This is the fourth drug discovery project funded by Families of SMA in 2013 with a total investment of $550,000. Elk Grove Village, IL (PRWEB) August 09, 2013 This program will systematically assess the effect of backbone chemistry on the therapeutic efficacy of Antisense...

2013-08-08 08:30:29

- PTC to Receive $10 Million Payment from Roche - SOUTH PLAINFIELD, N.J., Aug. 8, 2013 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced the selection of a development candidate in its spinal muscular atrophy (SMA) collaboration with Roche and the SMA Foundation. The achievement of the milestone triggers a $10 million payment to PTC from Roche. (Logo: http://photos.prnewswire.com/prnh/20010919/PTCLOGO) "We are excited about this important achievement in our...

2013-07-09 23:27:38

Scientist from preclinical CRO, PharmOptima, presents new assay at the 2013 International SMA Research Group Meeting. Portage, MI (PRWEB) July 09, 2013 "Spinal Muscular Atrophy (SMA) is a motor neuron disease. The motor neurons affect the voluntary muscles that are used for activities such as crawling, walking, head and neck control, and swallowing. It is a relatively common "rare disorder": approximately 1 in 6000 babies born are affected, and about 1 in 40 people are...

2013-06-06 23:01:33

Stories of Hope, Success and Progress Illustrate Need for Collaboration With Patients Horsham, Pa. (PRWEB) June 06, 2013 Utah Assistant Attorney General and spinal muscular atrophy survivor Steve Mikita and five other inspiring patient advocates will share stories of their tireless efforts to insert the patient voice at each step of the drug development process at the DIA 2013 49th Annual Meeting in Boston this month. The news media are invited to listen to the compelling stories of these...