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Latest Spinal muscular atrophy Stories

2014-01-22 00:21:53

SOUTH PLAINFIELD, N.J., Jan. 22, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT), the SMA Foundation, and Roche (SIX: RO, ROG; OTCQX: RHHBY), announced today that their joint research program in Spinal Muscular Atrophy (SMA) has entered the first stage of clinical development aiming to assess safety and tolerability of an oral compound in healthy volunteers. SMA is a genetic neuromuscular disorder that leads to muscle weakness and mobility impairment and is considered the...

2014-01-15 23:04:39

The organizations conceived the awards in order to draw strong, innovative talent into Spinal Muscular Atrophy research. Alexandria, VA (PRWEB) January 15, 2014 Two organizations, allied in the fight to defeat the deadly childhood disease spinal muscular atrophy (SMA), jointly announced this week the winners of the “FightSMA/Gwendolyn Strong Foundation Emerging Investigator Awards.” FightSMA and the Gwendolyn Strong Foundation conceived the awards in order to draw strong, innovative...

2013-12-18 15:08:14

Research team identified Neurexin2 as a novel target for potential therapy of neurodegeneration in Spinal Muscular Atrophy patients A recent study led by scientists from the National University of Singapore (NUS) opens a possible new route for treatment of Spinal Muscular Atrophy (SMA), a devastating disease that is the most common genetic cause of infant death and also affects young adults. As there is currently no known cure for SMA, the new discovery gives a strong boost to the fight...

2013-12-09 23:22:43

It describes the scientific strategy behind Antisense Drugs. It also provides updates on the ongoing research and clinical trials for this class of SMA drugs. Elk Grove Village, IL (PRWEB) December 09, 2013 Families of SMA has released a new edition of the Compass Newsletter, a publication dedicated to research updates. This newsletter was produced in a collaboration between Families of SMA, Biogen Idec, and Isis Pharmaceuticals. It describes the scientific strategy behind Antisense...

2013-11-18 23:24:29

FightSMA Thrilled to Make Announcement After Years of Advocacy by Families Across the U.S. Washington, DC (PRWEB) November 18, 2013 FightSMA (http://www.fightsma.org) is tremendously proud to announce that after years of passionate advocacy by families across the country the United States Senate passed the National Pediatric Research Network Act (NPRNA) Nov. 14 by unanimous consent.  The legislation, which the U.S. House approved on Tuesday, Nov.12, now heads to the President's...

2013-11-13 23:01:06

Bill authorizes the National Institutes of Health (NIH) to support the creation of up to 20 pediatric research consortia focused on diseases such as Spinal Muscular Atrophy. Washington, DC (PRWEB) November 13, 2013 National legislation to advance spinal muscular atrophy research took a giant leap forward on Tuesday, Nov. 12, 2013 with the passage by the U.S. House of Representatives of the National Pediatric Research Network Act (NPRNA). The NPRNA has been supported by a coalition of...

2013-10-31 23:37:18

Stanton Smiles“Dr. Robert B Stanton DMD” and his friends are attending The Gala of Hope. A South Florida fundraising event with one goal: To fund a cure for Spinal Muscular Atrophy. Fort Lauderdale, FL (PRWEB) October 31, 2013 In his never-ending pursuit to help his community, Dr. Robert B Stanton is joining the fight against Spinal Muscular Atrophy (SMA) by donating a Zoom Whitening Treatment, buying tickets to the Gala and participating in the auction. The money raised from his...


Word of the Day
barghest
  • A goblin in English folklore, often appearing in the shape of a large dog and believed to portend imminent death or misfortune.
  • A ghost, wraith, hobgoblin, elf, or spirit.
The origin of 'barghest' is not known, but it may be from perhaps burh-ghest, town-ghost, or German Berg-geist (mountain spirit) or Bär-geist (bear-spirit).
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