Latest Wiskott-Aldrich syndrome Stories
The virus that causes AIDS has been used to cure a pair of different genetic diseases, according to research published Thursday in the journal Science.
BOSTON, July 21, 2011 /PRNewswire-USNewswire/ -- The U.S. Food & Drug Administration (FDA) approved the launching in the U.S. of a clinical trial for gene therapy for a rare immunodeficiency, Wiskott-Aldrich syndrome (WAS).
--Immunotherapy Used in Proof-of-Principle Treatment for Wiskott-Aldrich Syndrome at The Children's Hospital of Philadelphia-- PHILADELPHIA, April 14, 2011 /PRNewswire-USNewswire/ -- In a novel approach that works around the gene defect in Wiskott-Aldrich syndrome, an inherited immune deficiency disorder, researchers used an alternative cell signaling pathway to significantly improve immune function in a 13-year-old boy with the disease.
--Dr. Jordan Orange, Holder of Newly Endowed Chair at The Children's Hospital of Philadelphia, Researches Immune Disorders-- PHILADELPHIA, Feb.
A pediatric immunologist at The Children's Hospital of Philadelphia collaborated with European gene therapy researchers who achieved marked clinical improvements in two young children with Wiskott-Aldrich syndrome, a very rare but often severe immunodeficiency disorder.
--Two Boys with Wiskott-Aldrich Syndrome Show Marked Improvement in European Study -- PHILADELPHIA, Nov.
Notch signaling helps determine the fate of a number of different cell types in a variety of organisms, including humans.